Registration is open here (early bird deadline: January 31st, 2024)

Don’t miss the unique opportunity to be part of a transformative event that is paving the way for advancements, collaborations, and hope in the realm of rare diseases organized by Rare Diseases Greece (RDG), member of EURORDIS-Rare Diseases Europe and Boussias Events following the World Rare Disease Day 2024.

Under the theme “Navigating the Uncharted: Advancements, Collaborations, and Hope in Rare Diseases”, the International Congress on Rare Diseases and Orphan Drugs aspires to stimulate dialogue and cooperation across all stakeholders – patient representatives, policymakers, clinicians, researchers, industry, payers and regulators – towards advancing a comprehensive rare disease strategy that promotes sustainability and equity within healthcare ecosystems.

IHI – call 6
IHI – call 6 is a two-stage call for proposals with the following topics:

• Topic 1: Support healthcare system resilience through a focus on persistency in the treatment of chronic diseases
• Topic 2: Development of evidence based practical guidance for sponsors on the use of real-world data / real-world evidence

Deadline for short proposals: 16 April 2024 at 17:00 Brussels time
Deadline for full proposals: 10 October 2024 at 17:00 Brussels time
Call web page: https://europa.eu/!RjXdcH

IHI – call 7
IHI – call 7 is a single-stage call for proposals with the following topics:

• Topic 1: Improving clinical management of heart disease from early detection to treatment
• Topic 2: User-centric technologies and optimised hospital workflows for a sustainable healthcare workforce
• Topic 3: Clinical validation of biomarkers for diagnosis, monitoring disease progression and treatment response

Deadline for full proposals: 22 May 2024 at 17:00 Brussels time.
Call web page: https://europa.eu/!64yx8Y

Find out more
All topic texts, call documentation (including a comprehensive guide for applicants), details of how to apply and guidance on how to find project partners can be found on the IHI website.

Info sessions and networking
The IHI Call Days for calls 6 & 7 are running from 10 January to 25 January 2024 inclusive. They include info sessions on the topics, our rules & procedures, and preparing the financial parts of the proposal, as well as pitching sessions on the topics. Participants can also use the Call Days website to identify and meet potential project partners. The recordings of these info sessions are also available online. Find out more: https://europa.eu/!RTJc7m

Why apply?
IHI calls for proposals represent an excellent opportunity for researchers to take part in ground-breaking cross-sector collaborative projects that aim to deliver tangible benefits for patients. Scientists from academia, diverse industry sectors, SMEs, mid-sized companies, hospitals and patients’ organisations are encouraged to get involved in our projects.

Pre-proposals must be submitted no later than 12:00h C.E.T. on March 5, 2024, via the electronic submission tool.

Funding: The total made available for this call is about 18 million euros.

Call text, participating countries and more information here.

The European Partnership for Personalised Medicine (EP PerMed), supported by the European Union under Horizon Europe (Grant Agreement N° 101137129), launches its first joint transnational call (JTC2024) for proposals on “Identification or Validation of Targets for Personalised Medicine Approaches (PMTargets)”. In total, 39 funding organisations participate in this call with an available budget of over 45 Mio€.

Timeline, contact, and more information here.

MARFANS, the French patient association for Marfan and related syndromes, is pleased to announce its first scientific and prospective meeting, Marfans 2035, on April 5th, 2024 which aims to learn about the main research directions in Marfan and related syndromes in the next 10 years, to exchange with researchers and clinicians, and to identify translational projects that could benefit from the support of the association.

Deadline for abstract submission : January 5, 2024 (marfans2035@gmail.com)

Confirmed speakers :

• Pr Julie de Backer, Ghent University Hospital – UZ Gent
• Pr Guillaume Jondeau, CNMR Syndrome de Marfan et apparentés, Service de cardiologie CHU Paris Nord-Val de Seine
• Dr Gisela Teixido Tura, Main researcher Cardiovascular Diseases, Vall Hebron Institut de Recerca, Barcelona
• Vivian de Waard, PhD, Associate Professor, Dept. Medical Biochemistry, Amsterdam UMC

Marfans association can actively support your research project in many ways: by bringing the patient perspective and being involved in your clinical trials and research protocols design, in helping in the administrative part of the preparation of the clinical trials applications and informed consent forms, in identifying eligible patients and facilitating recruitment, and ultimately by providing financial aid.

Should you be actively engaged in translational research projects that would that help treating,managing and reducing the symptomatic expression of the disease and benefit patients, we are pleased to invite you to submit an abstract of your presentation proposal.

Selected presentations will be in English, of 15’, and will have to outline :

• Your research goals in the next 10 years and expected outcomes for patients
• Estimated budgets for 10 years and co-financing needs
• Topics :
  • Therapeutic treatments : drug discovery and development, surgical interventions
  • Diagnostic
  • Diseases Prevention and Prediction
  • Care pathways
  • Genomics, gene therapy, etc

When and where?

18 December 2023 in Bari, Italy at Università degli Studi di Bari Aldo Moro (Dipartimento di Farmacia – Scienze del Farmaco) and online.

What will the speakers discuss about?

The following keynote topics around repurposing will be addressed:

• Current and proposed regulatory provisions in Europe for Research & Development and marketing authorisation;
• Industry and academic approaches to repurposing;
• Commercial perspectives and strategies to repurposing drugs;
• The meaning of repurposing in the paediatric context;
• Need for specific formulations to comply with the patient needs;
• Tools supporting Research & Development of repurposed drugs, like in silico approaches and real world data;
• Possible impact of changes proposed to the pharmaceutical legislation under Articles 48 and 75 of the proposed Regulation.

How to participate? 

Register here by 4th December. 

The course is free of charge for students, researchers, representatives from patients’ associations and not for profit organisations.

A registration fee is foreseen for participants from companies and for-profit organisations only. 10% discount will be applied if you register by 19th November.

For any enquiry, please contact info@benzifoundation.org    

Day 1: Deep dive into the EMA qualification procedure with a focus on registries – closed workshop in person and online, targeting regulators, registry holders and industry; 

Day 2: Establish the value of patient registries for regulatory decision-making – broad representation of stakeholders in person and online. To enable wide participation, some parts of the workshop will be broadcast.
More information on how to register for online participation on Day 2 will be published shortly.

Should you have any questions, feel free to contact them at emaregistries@ema.europa.eu.

More information here

Procure4Health is organising a webinar for the 2nd Call for Twinnings practical session and Challenge identification on November 2nd, 2023.
By joining this webinar you will get the chance to:

– Get to know more about the programme and application process

– Receive advice to prepare a good proposal to apply for the 2nd Call for Twinnings

– Find out how to identify a suitable partner for your proposal

– Learn from the experience of NAVARRABIOMED, which was awarded in the 1st Call for Twinnings

More information here

RARE2023 is honored to welcome world-renowned speakers from 15 different countries, all of whom are experts in the field of Rare Diseases, who will present ground-breaking and cutting-edge news on diagnosis, treatments and networking in Rare Diseases.

Among the new topics of RARE2023 are autoimmune disorders, palliative care in rare disease, surgical procedures in ultra-rare disorders, and newly approved innovative therapies for genetic and non-genetic rare diseases.

Register here before 9 November 2023 (followed by late and on-site registration)